Targeting a Pre-existing Anti-transgene T Cell Response for Effective Gene Therapy of MPS-I in the Mouse Model of the Disease-Reference-Cited by-同舟云学术

Targeting a Pre-existing Anti-transgene T Cell Response for Effective Gene Therapy of MPS-I in the Mouse Model of the Disease

Published:2019-07 Issue:7 Volume:27 Page:1215-1227
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Squeri Giorgia,Passerini Laura,Ferro Francesca,Laudisa Cecilia,Tomasoni Daniela,Deodato Federica,Donati Maria Alice,Gasperini Serena,Aiuti Alessandro,Bernardo Maria Ester,Gentner Bernhard,Naldini Luigi,Annoni Andrea,Biffi Alessandra,Gregori Silvia

Funder

Telethon Foundation

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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