Targeting a Pre-existing Anti-transgene T Cell Response for Effective Gene Therapy of MPS-I in the Mouse Model of the Disease-Reference-Cited by-同舟云学术

Targeting a Pre-existing Anti-transgene T Cell Response for Effective Gene Therapy of MPS-I in the Mouse Model of the Disease

Published:2019-07 Issue:7 Volume:27 Page:1215-1227
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Squeri Giorgia,Passerini Laura,Ferro Francesca,Laudisa Cecilia,Tomasoni Daniela,Deodato Federica,Donati Maria Alice,Gasperini Serena,Aiuti Alessandro,Bernardo Maria Ester,Gentner Bernhard,Naldini Luigi,Annoni Andrea,Biffi Alessandra,Gregori Silvia

Funder

Telethon Foundation

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference61 articles.

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