Improved Titer and Gene Transfer by Lentiviral Vectors Using Novel, Small β-Globin Locus Control Region Elements-Reference-Cited by-同舟云学术

Improved Titer and Gene Transfer by Lentiviral Vectors Using Novel, Small β-Globin Locus Control Region Elements

Published:2020-01 Issue:1 Volume:28 Page:328-340
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Morgan Richard A.,Unti Mildred J.,Aleshe Bamidele,Brown Devin,Osborne Kyle S.,Koziol Colin,Ayoub Paul G.,Smith Oliver B.,O’Brien Rachel,Tam Curtis,Miyahira Eric,Ruiz Marlene,Quintos Jason P.,Senadheera Shantha,Hollis Roger P.,Kohn Donald B.

Funder

Biomarin Pharmaceutical, Inc.

NIH/NHLBI

PhRMA Foundation Paul Calabresi Predoctoral Fellowship

UCLA

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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