Sustained phenotypic correction of hemophilia a mice following oncoretroviral-mediated expression of a bioengineered human factor VIII gene in long-term hematopoietic repopulating cells-Reference-Cited by-同舟云学术

Sustained phenotypic correction of hemophilia a mice following oncoretroviral-mediated expression of a bioengineered human factor VIII gene in long-term hematopoietic repopulating cells

Published:2004-11 Issue:5 Volume:10 Page:892-902
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Moayeri Morvarid,Ramezani Ali,Morgan Richard A.,Hawley Teresa S.,Hawley Robert G.

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference52 articles.

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4. Gene transfer as an approach to treating hemophilia;High;Circ. Res.,2001

5. Progress toward vector design for hematopoietic stem cell gene therapy;Hawley;Curr. Gene Ther.,2001

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