Toward a Gene Therapy for Dominant Disease: Validation of an RNA Interference-Based Mutation-Independent Approach-Reference-Cited by-同舟云学术

Toward a Gene Therapy for Dominant Disease: Validation of an RNA Interference-Based Mutation-Independent Approach

Published:2005-09 Issue:3 Volume:12 Page:555-561
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Kiang Anna-Sophia,Palfi Arpad,Ader Marius,Kenna Paul F.,Millington-Ward Sophia,Clark Gerry,Kennan Avril,O'Reilly Mary,Tam Lawrence C.T.,Aherne Aileen,McNally Niamh,Humphries Pete,Farrar G. Jane

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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2. Validation in mesenchymal progenitor cells of a mutation-independent ex vivo approach to gene therapy for osteogenesis imperfecta;Millington-Ward;Hum. Mol. Genet.,2002

3. On the genetics of retinitis pigmentosa and on mutation-independent approaches to therapeutic intervention;Farrar;EMBO J.,2002

4. RNAi of COL1A1 in mesenchymal progenitor cells;Millington-Ward;Eur. J. Hum. Genet.,2004

5. The RNAi revolution;Novina;Nature,2004

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