Iduronate-2-Sulfatase with Anti-human Transferrin Receptor Antibody for Neuropathic Mucopolysaccharidosis II: A Phase 1/2 Trial-Reference-Cited by-同舟云学术

Iduronate-2-Sulfatase with Anti-human Transferrin Receptor Antibody for Neuropathic Mucopolysaccharidosis II: A Phase 1/2 Trial

Published:2019-02 Issue:2 Volume:27 Page:456-464
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Okuyama Torayuki,Eto Yoshikatsu,Sakai Norio,Minami Kohtaro,Yamamoto Tatsuyoshi,Sonoda Hiroyuki,Yamaoka Mariko,Tachibana Katsuhiko,Hirato Tohru,Sato Yuji

Funder

JCR Pharmaceuticals

Sanofi

GC Pharma

Dainippon Sumitomo Pharma

Actelion

Alexion

Anges

BioMarin Pharmaceutical Inc.

Shire

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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5. A phase II/III clinical study of enzyme replacement therapy with idursulfase in mucopolysaccharidosis II (Hunter syndrome);Muenzer;Genet. Med.,2006

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