Current Clinical Applications of In Vivo Gene Therapy with AAVs-Reference-Cited by-同舟云学术

Current Clinical Applications of In Vivo Gene Therapy with AAVs

Published:2021-02 Issue:2 Volume:29 Page:464-488
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Mendell Jerry R.,Al-Zaidy Samiah A.,Rodino-Klapac Louise R.,Goodspeed Kimberly,Gray Steven J.,Kay Christine N.,Boye Sanford L.,Boye Shannon E.,George Lindsey A.,Salabarria Stephanie,Corti Manuela,Byrne Barry J.,Tremblay Jacques P.^ORCID

Funder

Canadian Institutes of Health Research

National Institutes of Health

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference262 articles.

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