Transcriptional reprogramming restores UBE3A brain-wide and rescues behavioral phenotypes in an Angelman syndrome mouse model-Reference-Cited by-同舟云学术

Transcriptional reprogramming restores UBE3A brain-wide and rescues behavioral phenotypes in an Angelman syndrome mouse model

Published:2023-04 Issue:4 Volume:31 Page:1088-1105
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

O’Geen Henriette,Beitnere Ulrika,Garcia Miranda S.,Adhikari Anna,Cameron David L.,Fenton Timothy A.,Copping Nycole A.,Deng Peter,Lock Samantha,Halmai Julian A.N.M.,Villegas Isaac J.,Liu Jiajian,Wang Danhui,Fink Kyle D.,Silverman Jill L.,Segal David J.

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference74 articles.

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5. Recovery of Angelman syndrome rat deficits with UBE3A protein supplementation;Dodge;Mol. Cell. Neurosci.,2022

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