CRISPR/Cas9-Mediated In Situ Correction of LAMB3 Gene in Keratinocytes Derived from a Junctional Epidermolysis Bullosa Patient-Reference-Cited by-同舟云学术

CRISPR/Cas9-Mediated In Situ Correction of LAMB3 Gene in Keratinocytes Derived from a Junctional Epidermolysis Bullosa Patient

Published:2018-11 Issue:11 Volume:26 Page:2592-2603
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Benati Daniela,Miselli Francesca,Cocchiarella Fabienne,Patrizi Clarissa,Carretero Marta,Baldassarri Samantha,Ammendola Virginia,Has Cristina,Colloca Stefano,Del Rio Marcela,Larcher Fernando,Recchia Alessandra

Funder

European Commission

Italian Ministry of University and Research

Ministry of Economy and Competitiveness

Instituto de Salud Carlos III

European Regional Development Funds (ERDF

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference49 articles.

1. Corrective transduction of human epidermal stem cells in laminin-5-dependent junctional epidermolysis bullosa;Dellambra;Hum. Gene Ther.,1998

2. Somatic correction of junctional epidermolysis bullosa by a highly recombinogenic AAV variant;Melo;Mol. Ther.,2014

3. Correction of junctional epidermolysis bullosa by transplantation of genetically modified epidermal stem cells;Mavilio;Nat. Med.,2006

4. Regeneration of the entire human epidermis using transgenic stem cells;Hirsch;Nature,2017

5. Safety and wound outcomes following genetically corrected autologous epidermal grafts in patients with recessive dystrophic epidermolysis bullosa;Siprashvili;JAMA,2016

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