Gene editing of hematopoietic stem cells restores T-cell response in familial hemophagocytic lymphohistiocytosis
Author:
Funder
Albert-Ludwigs-Universität Freiburg
Deutsche Forschungsgemeinschaft
Publisher
Elsevier BV
Subject
Immunology,Immunology and Allergy
Reference57 articles.
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2. Hemophagocytic syndromes—an update;Janka;Blood Rev,2014
3. Cytotoxic granule secretion by lymphocytes and its link to immune homeostasis;de Saint Basile;F1000Res,2015
4. Genetic and mechanistic diversity in pediatric hemophagocytic lymphohistiocytosis;Chinn;Blood,2018
5. Stem cell transplantation for children with hemophagocytic lymphohistiocytosis: results from the HLH-2004 study;Bergsten;Blood Adv,2020
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