Effects of asfotase alfa in adults with pediatric-onset hypophosphatasia over 24 months of treatment
Author:
Funder
Alexion Pharmaceuticals
Publisher
Elsevier BV
Subject
Histology,Physiology,Endocrinology, Diabetes and Metabolism
Reference24 articles.
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2. Hypophosphatasia—aetiology, nosology, pathogenesis, diagnosis and treatment;Whyte;Nat. Rev. Endocrinol.,2016
3. Hypophosphatasia: a unique disorder of bone mineralization;Villa-Suárez;Int. J. Mol. Sci.,2021
4. Burden of disease in adult patients with hypophosphatasia: results from two patient-reported surveys;Weber;Metabolism,2016
5. Burden of illness in adults with hypophosphatasia: data from the Global Hypophosphatasia Patient Registry;Seefried;J. Bone Miner. Res.,2020
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1. Efficacy and safety of asfotase alfa in patients with hypophosphatasia: A systematic review;Bone;2024-11
2. Challenges in Hypophosphatasia: Suspicion, Diagnosis, Genetics, Management, and Follow-Up;Hormone Research in Paediatrics;2024-08-05
3. Enzyme replacement therapy for hypophosphatasia—The current paradigm;Clinical Endocrinology;2024-07-14
4. Improvement in quality of life after asfotase alfa treatment in adults with pediatric-onset hypophosphatasia: data from 5 patient-reported outcome measures;JBMR Plus;2024-05-07
5. Diagnosis and treatment of adult hypophosphatasia: Still a big challenge?;Osteoporosis and Sarcopenia;2024-03
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