Advances in the Therapy of Spinal Muscular Atrophy

Author:

Klotz JennaORCID,Tesi Rocha Carolina,Dunaway Young SallyORCID,Duong Tina,Buu MyMy,Sampson Jacinda,Day John W.ORCID

Publisher

Elsevier BV

Subject

Pediatrics, Perinatology and Child Health

Cited by 6 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献

1. Measuring Fatigue and Fatigability in Spinal Muscular Atrophy (SMA): Challenges and Opportunities;Journal of Clinical Medicine;2023-05-14

2. On the path to evidence-based therapy in neuromuscular disorders;Motor System Disorders, Part I: Normal Physiology and Function and Neuromuscular Disorders;2023

3. Childhood spinal muscular atrophy;Handbook of Clinical Neurology;2023

4. Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2): secondary analyses from an open-label trial;The Lancet Neurology;2022-12

5. New treatments in spinal muscular atrophy;Archives of Disease in Childhood;2022-10-31

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