Enzyme replacement therapy and monitoring for children with type 1 Gaucher disease: consensus recommendations-Reference-Cited by-同舟云学术

Enzyme replacement therapy and monitoring for children with type 1 Gaucher disease: consensus recommendations

Published:2004-01 Issue:1 Volume:144 Page:112-120
ISSN:0022-3476
Container-title:The Journal of Pediatrics
language:en
Short-container-title:The Journal of Pediatrics

Author:

Charrow Joel,Andersson Hans C.,Kaplan Paige,Kolodny Edwin H.,Mistry Pramod,Pastores Gregory,Prakash-Cheng Ainu,Rosenbloom Barry E.,Scott C.Ronald,Wappner Rebecca S.,Weinreb Neal J.

Publisher

Elsevier BV

Subject

Pediatrics, Perinatology, and Child Health

Reference72 articles.

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2. Short communications: a deficiency of glucocerebrosidase in Gaucher disease;Patrick;Biochem J,1965

3. Gaucher disease: a century of delineation and understanding;Desnick;Prog Clin Biol Res,1982

4. Pathology of the Gaucher cell;Parkin;Prog Clin Biol Res,1982

5. Enzyme therapy in type 1 Gaucher disease: comparative efficacy of mannose-terminated glucocerebrosidase from natural and recombinant sources;Grabowski;Ann Intern Med,1995

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