A Review of Methodological Considerations for Economic Evaluations of Gene Therapies and Their Application in Literature-Reference-Cited by-同舟云学术

A Review of Methodological Considerations for Economic Evaluations of Gene Therapies and Their Application in Literature

Published:2020-09 Issue:9 Volume:23 Page:1268-1280
ISSN:1098-3015
Container-title:Value in Health
language:en
Short-container-title:Value in Health

Author:

ten Ham Renske M.T.,Klungel Olaf H.,Leufkens Hubert G.M.,Frederix Geert W.J.

Publisher

Elsevier BV

Subject

Public Health, Environmental and Occupational Health,Health Policy

Reference64 articles.

1. From clinical trials to clinical practice: practical considerations for gene replacement therapy in SMA type 1;Al-Zaidy;Pediatr Neurol,2019

2. Technology forecast: advanced therapies in late clinical research, EMA approval or clinical application via hospital exemption;Eder;J Mark Access Health Policy,2019

3. Health technology assessment of gene therapies for inherited genetic disorders in the US and Europe;Hollier-Hann;Value Health,2018

4. Market access of ATMPs: overview and expected challenges;Hanna;Value Health,2015

5. Addressing the value of gene therapy and enhancing patient access to transformative treatments;Salzman;Mol Ther,2018

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1. Market Access Challenges and Solutions in Cell and Gene Therapy in The Netherlands;Journal of Market Access & Health Policy;2024-07-30

2. Surrogacy and the Valuation of ATMPs: Taking Our Place in the Evidence Generation/Assessment Continuum;PharmacoEconomics;2023-11-22

3. Using Real-World Data to Inform Value-Based Contracts for Cell and Gene Therapies in Medicaid;PharmacoEconomics;2023-11-21

4. How are health technology assessment bodies responding to the assessment challenges posed by cell and gene therapy?;BMC Health Services Research;2023-05-13

5. Recommendations for economic evaluations of cell and gene therapies: a systematic literature review with critical appraisal;Expert Review of Pharmacoeconomics & Outcomes Research;2023-04-19