The evolving landscape of gene therapy for congenital haemophilia: An unprecedented, problematic but promising opportunity for worldwide clinical studies
Author:
Publisher
Elsevier BV
Subject
Oncology,Hematology
Reference97 articles.
1. Definitions in hemophilia;White,2001
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3. Awareness of individual goals, preferences, and priorities of persons with severe congenital haemophilia A for a tailored shared decision-making approach to liver-directed gene therapy. A practical guideline;Blood Reviews;2023-11
4. From a bispecific monoclonal antibody to gene therapy: A new era in the treatment of hemophilia A;Biomedical Papers;2023-03-15
5. Progress, and prospects in the therapeutic armamentarium of persons with congenital hemophilia. Defining the place for liver-directed gene therapy;Blood Reviews;2023-03
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