Dystrophin Restoration after Adeno-Associated Virus U7–Mediated Dmd Exon Skipping Is Modulated by Muscular Exercise in the Severe D2-Mdx Duchenne Muscular Dystrophy Murine Model-Reference-Cited by-同舟云学术

Dystrophin Restoration after Adeno-Associated Virus U7–Mediated Dmd Exon Skipping Is Modulated by Muscular Exercise in the Severe D2-Mdx Duchenne Muscular Dystrophy Murine Model

Published:2022-11 Issue:11 Volume:192 Page:1604-1618
ISSN:0002-9440
Container-title:The American Journal of Pathology
language:en
Short-container-title:The American Journal of Pathology

Author:

Monceau Alexandra^ORCID,Moutachi Dylan,Lemaitre Mégane,Garcia Luis,Trollet Capucine^ORCID,Furling Denis,Klein Arnaud,Ferry Arnaud^ORCID

Publisher

Elsevier BV

Subject

Pathology and Forensic Medicine

Reference40 articles.

1. DMD transcript imbalance determines dystrophin levels;Spitali;FASEB J,2013

2. Systemic AAV micro-dystrophin gene therapy for Duchenne muscular dystrophy;Duan;Mol Ther,2018

3. Gene therapy for muscular dystrophy: current progress and future prospects;Trollet;Expert Opin Biol Ther,2009

4. Rescue of dystrophic muscle through U7 snRNA-mediated exon skipping;Goyenvalle;Science,2004

5. Development of novel micro-dystrophins with enhanced functionality;Ramos;Mol Ther,2019

Cited by 6 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Treadmill running and mechanical overloading improved the strength of the plantaris muscle in the dystrophin‐desmin double knockout (DKO) mouse;The Journal of Physiology;2024-07-09

2. Design and evaluation of antisense sequence length for modified mouse U7 small nuclear RNA to induce efficient pre-messenger RNA splicing modulation in vitro;PLOS ONE;2024-07-09

3. Molecular and Biochemical Therapeutic Strategies for Duchenne Muscular Dystrophy;Neurology International;2024-07-05

4. Beneficial effects of resistance training on both mild and severe mouse dystrophic muscle function as a preclinical option for Duchenne muscular dystrophy;PLOS ONE;2024-03-08

5. RNA-Based Therapeutic Technology;International Journal of Molecular Sciences;2023-10-16