Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B): 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial-Reference-Cited by-同舟云学术

Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B): 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial

Published:2024-04 Issue:4 Volume:11 Page:e265-e275
ISSN:2352-3026
Container-title:The Lancet Haematology
language:en
Short-container-title:The Lancet Haematology

Author:

Coppens Michiel,Pipe Steven W,Miesbach Wolfgang,Astermark Jan,Recht Michael,van der Valk Paul,Ewenstein Bruce,Pinachyan Karen,Galante Nicholas,Le Quellec Sandra,Monahan Paul E,Leebeek Frank W G,Castaman Giancarlo,Crary Shelley E,Escobar Miguel,Gomez Esteban,Haley Kristina M,Hermans Cedric R J R,Kampmann Peter,Kazmi Rashid,Key Nigel S,Klamroth Robert,Konkle Barbara A,Kruse-Jarres Rebecca,Lattimore Susan,Lemons Richard,Meijer Karina,O'Connell Niamh,Quon Doris V,Raheja Priyanka,Symington Emily,Verhamme Peter,Visweshwar Nathan,von Drygalski Annette,Wang Michael,Wheeler Allison P,White Shanna,Young Guy

Funder

CSL Behring

Publisher

Elsevier BV

Reference33 articles.

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4. WFH guidelines for the management of hemophilia, 3rd edition. Chapter 6: prophylaxis in Hemophilia;Carcao;Haemophilia,2020

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1. Biological Barriers for Drug Delivery and Development of Innovative Therapeutic Approaches in HIV, Pancreatic Cancer, and Hemophilia A/B;Pharmaceutics;2024-09-13

2. Gene Therapy for Hemophilia B: Achievements, Open Issues, and Perspectives;Seminars in Thrombosis and Hemostasis;2024-05-31

3. Hämophilie-Behandlung in Österreich;Wiener klinische Wochenschrift;2024-05

4. Breaking ground in haemophilia B gene therapy: insights from the HOPE-B trial and beyond;The Lancet Haematology;2024-04