In Situ Gene Therapy via AAV-CRISPR-Cas9-Mediated Targeted Gene Regulation-Reference-Cited by-同舟云学术

In Situ Gene Therapy via AAV-CRISPR-Cas9-Mediated Targeted Gene Regulation

Published:2018-07 Issue:7 Volume:26 Page:1818-1827
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Moreno Ana M.,Fu Xin,Zhu Jie,Katrekar Dhruva,Shih Yu-Ru V.,Marlett John,Cabotaje Jessica,Tat Jasmine,Naughton John,Lisowski Leszek,Varghese Shyni,Zhang Kang,Mali Prashant

Funder

UCSD Institutional Funds

Burroughs Wellcome Fund

March of Dimes Foundation

Kimmel Foundation

NIH

CONACYT

UCMEXUS

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference59 articles.

1. Biotechnology: rewriting a genome;Charpentier;Nature,2013

2. Efficient genome editing in zebrafish using a CRISPR-Cas system;Hwang;Nat. Biotechnol.,2013

3. Heritable gene targeting in the mouse and rat using a CRISPR-Cas system;Li;Nat. Biotechnol.,2013

4. Cas9 as a versatile tool for engineering biology;Mali;Nat. Methods,2013

5. RNA-guided human genome engineering via Cas9;Mali;Science,2013

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