Subject
Pediatrics, Perinatology and Child Health
Reference29 articles.
1. Spinal muscular atrophy;Lunn;Lancet Lond Engl,2008
2. Effects of nusinersen after one year of treatment in 123 children with SMA type 1 or 2: a French real-life observational study;Audic;Orphanet J Rare Dis,2020
3. Health & Medicine présenté à;Disponible sur,2021
4. Spinal muscular atrophy;Arnold;Handb Clin Neurol,2018
5. Pharmacokinetics of phosphorothioate antisense oligodeoxynucleotides;Geary;Curr Opin Investig Drugs,2001