Proliferation deficiency of multipotent hematopoietic progenitors in ribosomal protein S19 (RPS19)-deficient diamond–Blackfan anemia improves following RPS19 gene transfer-Reference-Cited by-同舟云学术

Proliferation deficiency of multipotent hematopoietic progenitors in ribosomal protein S19 (RPS19)-deficient diamond–Blackfan anemia improves following RPS19 gene transfer

Published:2003-05 Issue:5 Volume:7 Page:613-622
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Hamaguchi Isao,Flygare Johan,Nishiura Hiroshi,Brun Ann C.M,Ooka Andreas,Kiefer Thomas,Ma Zhi,Dahl Niklas,Richter Johan,Karlsson Stefan

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference39 articles.

1. Congenital hypoplastic anemia;Diamond;Adv. Pediatr.,1976

2. The bone marrow failure syndromes;Alter,1998

3. Diamond–Blackfan anemia;Halperin;Am. J. Pediatr. Hematol. Oncol.,1989

4. In vitro growth and regulation of bone marrow enriched CD34+ hematopoietic progenitors in Diamond–Blackfan anemia;Bagnara;Blood,1991

5. Chromosomal aberrations in two cases of inherited aplastic anemia with unusual clinical features;Hirschman;Ann. Intern. Med.,1969

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