Progress in treating inherited retinal diseases: Early subretinal gene therapy clinical trials and candidates for future initiatives-Reference-Cited by-同舟云学术

Progress in treating inherited retinal diseases: Early subretinal gene therapy clinical trials and candidates for future initiatives

Published:2020-07 Issue: Volume:77 Page:100827
ISSN:1350-9462
Container-title:Progress in Retinal and Eye Research
language:en
Short-container-title:Progress in Retinal and Eye Research

Author:

Garafalo Alexandra V.,Cideciyan Artur V.,Héon Elise,Sheplock Rebecca,Pearson Alexander,WeiYang Yu Caberry^ORCID,Sumaroka Alexander,Aguirre Gustavo D.,Jacobson Samuel G.^ORCID

Funder

National Institutes of Health/National Eye Institute

Publisher

Elsevier BV

Subject

Sensory Systems,Ophthalmology

Reference239 articles.

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5. AAV2-hCHM subretinal delivery to the macular in choroideremia: 2 year results of an ongoing phase I/II gene therapy trial;Aleman;Investig. Ophthalmol. Vis. Sci.,2019

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