Safety of rAAV2/2- ND4 Gene Therapy for Leber Hereditary Optic Neuropathy-Reference-Cited by-同舟云学术

Safety of rAAV2/2- ND4 Gene Therapy for Leber Hereditary Optic Neuropathy

Published:2018-06 Issue:6 Volume:125 Page:945-947
ISSN:0161-6420
Container-title:Ophthalmology
language:en
Short-container-title:Ophthalmology

Author:

Vignal Catherine,Uretsky Scott^ORCID,Fitoussi Serge,Galy Anne,Blouin Laure,Girmens Jean-François,Bidot Samuel,Thomasson Nitza,Bouquet Céline,Valero Sonia,Meunier Sandrine,Combal Jean-Philippe^ORCID,Gilly Bernard,Katz Barrett,Sahel José-Alain

Publisher

Elsevier BV

Subject

Ophthalmology

Reference5 articles.

1. Leber hereditary optic neuropathy: bringing the lab to the clinic;Rasool;Semin Ophthalmol,2016

2. Leber hereditary optic neuropathy;Yu-Wai-Man;J Med Genet,2002

3. Nuclear expression of mitochondrial ND4 leads to the protein assembling in complex I and prevents optic atrophy and visual loss;Cwerman-Thibault;Mol Ther Methods Clin Dev,2015

4. Safety and effects of the vector for the Leber hereditary optic neuropathy gene therapy clinical trial;Koilkonda;JAMA Ophthalmol,2014

5. LHON gene therapy vector prevents visual loss and optic neuropathy induced by G11778A mutant mitochondrial DNA: biodistribution and toxicology profile;Koilkonda;Invest Ophthalmol Vis Sci,2014

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