Efficacy and safety of empagliflozin in glycogen storage disease type Ib: Data from an international questionnaire-Reference-Cited by-同舟云学术

Efficacy and safety of empagliflozin in glycogen storage disease type Ib: Data from an international questionnaire

Published:2022-08 Issue:8 Volume:24 Page:1781-1788
ISSN:1098-3600
Container-title:Genetics in Medicine
language:en
Short-container-title:Genetics in Medicine

Author:

Grünert Sarah C.^ORCID,Derks Terry G.J.,Adrian Katarina,Al-Thihli Khalid,Ballhausen Diana,Bidiuk Joanna,Bordugo Andrea,Boyer Monica,Bratkovic Drago,Brunner-Krainz Michaela,Burlina Alberto,Chakrapani Anupam,Corpeleijn Willemijn,Cozens Alison,Dawson Charlotte,Dhamko Helena,Milosevic Maja Djordjevic,Eiroa Hernan,Finezilber Yael,Moura de Souza Carolina Fischinger,Garcia-Jiménez Maria Concepción,Gasperini Serena,Haas Dorothea,Häberle Johannes,Halligan Rebecca,Fung Law Hiu,Hörbe-Blindt Alexandra,Horka Laura Maria,Huemer Martina,Uçar Sema Kalkan,Kecman Bozica,Kilavuz Sebile,Kriván Gergely,Lindner Martin,Lüsebrink Natalia,Makrilakis Konstantinos,Mei-Kwun Kwok Anne,Maier Esther M.,Maiorana Arianna,McCandless Shawn E.,Mitchell John James,Mizumoto Hiroshi,Mundy Helen,Ochoa Carlos,Pierce Kathryn,Fraile Pilar Quijada,Regier Debra,Rossi Alessandro,Santer René,Schuman Hester C.,Sobieraj Piotr,Spenger Johannes,Spiegel Ronen,Stepien Karolina M.,Tal Galit,Tanšek Mojca Zerjav,Torkar Ana Drole,Tchan Michel,Thyagu Santhosh,Schrier Vergano Samantha A.,Vucko Erika,Weinhold Natalie,Zsidegh Petra,Wortmann Saskia B.

Publisher

Elsevier BV

Subject

Genetics (clinical)

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3. Neutropenia in glycogen storage disease Ib: outcomes for patients treated with granulocyte colony-stimulating factor;Dale;Curr Opin Hematol,2019

4. Neutropenia, neutrophil dysfunction, and inflammatory bowel disease in glycogen storage disease type Ib: results of the European Study on Glycogen Storage Disease type I;Visser;J Pediatr,2000

5. Glycogen storage diseases: diagnosis, treatment and outcome;Chen;Transl Sci Rare Dis,2016

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