Long-term safety and efficacy of pegunigalsidase alfa: A multicenter 6-year study in adult patients with Fabry disease
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Published:2023-12
Issue:12
Volume:25
Page:100968
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ISSN:1098-3600
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Container-title:Genetics in Medicine
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language:en
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Short-container-title:Genetics in Medicine
Author:
Hughes DerralynnORCID,
Gonzalez Derlis,
Maegawa Gustavo,
Bernat John A.,
Holida Myrl,
Giraldo Pilar,
Atta Mohamed G.,
Chertkoff Raul,
Alon Sari,
Almon Einat Brill,
Rocco Rossana,
Goker-Alpan Ozlem
Subject
Genetics (clinical)
Cited by
8 articles.
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