Subject
Genetics,Molecular Biology
Reference17 articles.
1. Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophy;Amoasii;Sci. Transl. Med.,2017
2. Gene editing restores dystrophin expression in a canine model of Duchenne muscular dystrophy;Amoasii;Science,2018
3. Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and neuromuscular, rehabilitation, endocrine, and gastrointestinal and nutritional management;Birnkrant;Lancet Neurol.,2018
4. The TREAT-NMD DMD Global Database: analysis of more than 7,000 Duchenne muscular dystrophy mutations;Bladen;Hum. Mutat.,2015
5. Easy quantitative assessment of genome editing by sequence trace decomposition;Brinkman;Nucleic Acids Res.,2014