If you build a rare disease registry, will they enroll and will they use it? Methods and data from the National Registry of Myotonic Dystrophy (DM) and Facioscapulohumeral Muscular Dystrophy (FSHD)-Reference-Cited by-同舟云学术

If you build a rare disease registry, will they enroll and will they use it? Methods and data from the National Registry of Myotonic Dystrophy (DM) and Facioscapulohumeral Muscular Dystrophy (FSHD)

Published:2012-03 Issue:2 Volume:33 Page:302-311
ISSN:1551-7144
Container-title:Contemporary Clinical Trials
language:en
Short-container-title:Contemporary Clinical Trials

Author:

Hilbert James E.,Kissel John T.,Luebbe Elizabeth A.,Martens William B.,McDermott Michael P.,Sanders Donald B.,Tawil Rabi,Thornton Charles A.,Moxley Richard T.

Publisher

Elsevier BV

Subject

Pharmacology (medical),General Medicine

Reference56 articles.

1. Myotonic Dystrophy;Harper,2001

2. Facioscapulohumeral disease University of Leiden;Padberg,1982

3. Facioscapulohumeral muscular dystrophy;Tawil;Muscle Nerve,2006

4. Myotonic dystrophy type 2: molecular, diagnostic and clinical spectrum;Day;Neurology,2003

5. Clinical and molecular aspects of the myotonic dystrophies: a review;Machuca-Tzili;Muscle Nerve,2005

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