Rycal S48168 (ARM210) for RYR1-related myopathies: a phase one, open-label, dose-escalation trial
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Published:2024-02
Issue:
Volume:68
Page:102433
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ISSN:2589-5370
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Container-title:eClinicalMedicine
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language:en
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Short-container-title:eClinicalMedicine
Author:
Todd Joshua J., Lawal Tokunbor A., Chrismer Irene C., Kokkinis Angela, Grunseich Christopher, Jain Minal S., Waite Melissa R., Biancavilla Victoria, Pocock Shavonne, Brooks Kia, Mendoza Christopher J., Norato Gina, Cheung Ken, Riekhof Willa, Varma Pooja, Colina-Prisco Claudia, Emile-Backer Magalie, Meilleur Katherine G., Marks Andrew R., Webb Yael, Marcantonio Eugene E.ORCID, Foley A. Reghan, Bönnemann Carsten G.ORCID, Mohassel PayamORCID
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