Cas9 protein delivery non-integrating lentiviral vectors for gene correction in sickle cell disease-Reference-Cited by-同舟云学术

Cas9 protein delivery non-integrating lentiviral vectors for gene correction in sickle cell disease

Published:2021-06 Issue: Volume:21 Page:121-132
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Uchida Naoya^ORCID,Drysdale Claire M.,Nassehi Tina^ORCID,Gamer Jackson^ORCID,Yapundich Morgan^ORCID,DiNicola Julia^ORCID,Shibata Yoshitaka^ORCID,Hinds Malikiya,Gudmundsdottir Bjorg^ORCID,Haro-Mora Juan J.,Demirci Selami,Tisdale John F.

Funder

National Heart, Lung, and Blood Institute

National Institute of Diabetes and Digestive and Kidney Diseases

National Institutes of Health

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

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