Improved engraftment and therapeutic efficacy by human genome-edited hematopoietic stem cells with Busulfan-based myeloablation
Author:
Funder
University of Pennsylvania The Orphan Disease Center
NIH
Publisher
Elsevier BV
Subject
Genetics,Molecular Biology,Molecular Medicine
Reference70 articles.
1. The changing landscape of gene editing in hematopoietic stem cells: a step towards Cas9 clinical translation;Dever;Curr. Opin. Hematol.,2017
2. A programmable dual-RNA-guided DNA endonuclease in adaptive bacterial immunity;Jinek;Science,2012
3. RNA-programmed genome editing in human cells;Jinek;Elife,2013
4. Gene editing on center stage;Bak;Trends Genet.,2018
5. BCL11A enhancer-edited hematopoietic stem cells persist in rhesus monkeys without toxicity;Demirci;J. Clin. Invest.,2020
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