Characterization of the humanized FRG mouse model and development of an AAV-LK03 variant with improved liver lobular biodistribution-Reference-Cited by-同舟云学术

Characterization of the humanized FRG mouse model and development of an AAV-LK03 variant with improved liver lobular biodistribution

Published:2023-03 Issue: Volume:28 Page:220-237
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Cabanes-Creus Marti,Navarro Renina Gale,Liao Sophia H.Y.,Scott Suzanne,Carlessi Rodrigo,Roca-Pinilla Ramon,Knight Maddison,Baltazar Grober,Zhu Erhua,Jones Matthew,Denisenko Elena,Forrest Alistair R.R.,Alexander Ian E.,Tirnitz-Parker Janina E.E.,Lisowski Leszek^ORCID

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

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