PAM-altering SNP-based allele-specific CRISPR-Cas9 therapeutic strategies for Huntington’s disease
Author:
Funder
CHDI Foundation
National Institutes of Health
NINDS
Harvard NeuroDiscovery Center
Publisher
Elsevier BV
Subject
Genetics,Molecular Biology,Molecular Medicine
Reference98 articles.
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4. The HTT CAG-expansion mutation determines age at death but not disease duration in Huntington disease;Keum;Am. J. Hum. Genet.,2016
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