Human Lentiviral Gene Therapy Restores the Cellular Phenotype of Autosomal Recessive Complete IFN-γR1 Deficiency-Reference-Cited by-同舟云学术

Human Lentiviral Gene Therapy Restores the Cellular Phenotype of Autosomal Recessive Complete IFN-γR1 Deficiency

Published:2020-06 Issue: Volume:17 Page:785-795
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Hahn Katharina,Pollmann Liart,Nowak Juliette,Nguyen Ariane Hai Ha,Haake Kathrin,Neehus Anna-Lena,Waqas Syed F. Hassnain,Pessler Frank,Baumann Ulrich,Hetzel Miriam,Casanova Jean-Laurent,Schulz Ansgar,Bustamante Jacinta,Ackermann Mania,Lachmann Nico

Funder

Else Krööner-Fresenius St Stiftung

the German Center for Infection Research

European Research Council

European Union’s Horizon 2020

Agence Nationale de la Recherche

Fondation Bettencourt Schueller

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference41 articles.

1. Hematopoietic Stem Cell Gene Therapy: Progress and Lessons Learned;Morgan;Cell Stem Cell,2017

2. Broadening the indications for hematopoietic stem cell genetic therapies;Williams;Cell Stem Cell,2013

3. Mendelian susceptibility to mycobacterial infection in man;Altare;Curr. Opin. Immunol.,1998

4. Interferon-γ-receptor deficiency in an infant with fatal bacille Calmette-Guérin infection;Jouanguy;N. Engl. J. Med.,1996

5. A mutation in the interferon-gamma-receptor gene and susceptibility to mycobacterial infection;Newport;N. Engl. J. Med.,1996

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