Efficacy and Safety of Glycosidic Enzymes for Improved Gene Delivery to the Retina following Intravitreal Injection in Mice
Author:
Funder
Medical Research Council
ERC
MRC
Publisher
Elsevier BV
Subject
Genetics,Molecular Biology,Molecular Medicine
Reference47 articles.
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4. Age-dependent effects of RPE65 gene therapy for Leber’s congenital amaurosis: a phase 1 dose-escalation trial;Maguire;Lancet,2009
5. Long-term effect of gene therapy on Leber’s congenital amaurosis;Bainbridge;N. Engl. J. Med.,2015
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