Persistent hematopoietic polyclonality after lentivirus-mediated gene therapy for Fabry disease-Reference-Cited by-同舟云学术

Persistent hematopoietic polyclonality after lentivirus-mediated gene therapy for Fabry disease

Published:2023-03 Issue: Volume:28 Page:262-271
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Saleh Amr H.^ORCID,Rothe Michael,Barber Dwayne L.,McKillop William M.,Fraser Graeme,Morel Chantal F.,Schambach Axel,Auray-Blais Christiane,West Michael L.,Khan Aneal,Fowler Daniel H.,Rupar C. Anthony,Foley Ronan,Medin Jeffrey A.,Keating Armand

Funder

Canadian Institutes of Health Research

Kidney Foundation of Canada

MACC Fund

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference26 articles.

1. Fabry's disease;Zarate;Lancet,2008

2. Fabry disease revisited: management and treatment recommendations for adult patients;Ortiz;Mol. Genet. Metab.,2018

3. Lentivirus-mediated gene therapy for Fabry disease;Khan;Nat. Commun.,2021

4. LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1;Hacein-Bey-Abina;Science,2003

5. Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1;Hacein-Bey-Abina;J. Clin. Invest.,2008

Cited by 4 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Anderson–Fabry disease management: role of the cardiologist;European Heart Journal;2024-03-15

2. Preclinical lentiviral vector-mediated hematopoietic stem and progenitor cell gene therapy corrects Pompe disease-related muscle and neurological manifestations;2023-11-05

3. A mass spectrometry assay for detection of endogenous and lentiviral engineered hemoglobin in cultured cells and sickle cell disease mice;The Journal of Gene Medicine;2023-07-17

4. Fabry disease: current treatment and future perspective;Journal of Genetic Medicine;2023-06-30