Systemic γ-sarcoglycan AAV gene transfer results in dose-dependent correction of muscle deficits in the LGMD 2C/R5 mouse model-Reference-Cited by-同舟云学术

Systemic γ-sarcoglycan AAV gene transfer results in dose-dependent correction of muscle deficits in the LGMD 2C/R5 mouse model

Published:2023-03 Issue: Volume:28 Page:284-299
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Seo Young-Eun,Baine Stephen H.,Kempton Amber N.,Rogers Oliver C.,Lewis Sarah,Adegboye Kaitlin,Haile Alex,Griffin Danielle A.,Peterson Ellyn L.,Pozsgai Eric R.,Potter Rachael A.,Rodino-Klapac Louise R.

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

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