Non-clinical Safety and Efficacy of an AAV2/8 Vector Administered Intravenously for Treatment of Mucopolysaccharidosis Type VI-Reference-Cited by-同舟云学术

Non-clinical Safety and Efficacy of an AAV2/8 Vector Administered Intravenously for Treatment of Mucopolysaccharidosis Type VI

Published:2017-09 Issue: Volume:6 Page:143-158
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Ferla Rita,Alliegro Marialuisa,Marteau Jean-Brice,Dell’Anno Margherita,Nusco Edoardo,Pouillot Severine,Galimberti Stefania,Valsecchi Maria Grazia,Zuliani Vincent,Auricchio Alberto

Funder

Fondazione Telethon

European Commission Seventh Framework Programme

MeuSIX

Isaac Foundation

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

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