Development of Intrathecal AAV9 Gene Therapy for Giant Axonal Neuropathy-Reference-Cited by-同舟云学术

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Development of Intrathecal AAV9 Gene Therapy for Giant Axonal Neuropathy

Published:2018-06 Issue: Volume:9 Page:160-171
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Bailey Rachel M.,Armao Diane,Nagabhushan Kalburgi Sahana,Gray Steven J.

Funder

Hannah’s Hope Fund

NIH National Institute of Neurological Disorders and Stroke

NIH National Institute of Child Health and Human Development

Research to Prevent Blindness

NCI Center Core

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference46 articles.

1. Giant axonal neuropathy—a unique case with segmental neurofilamentous masses;Asbury;Acta Neuropathol.,1972

2. Giant axonal neuropathy;Berg;Pediatrics,1972

3. Giant axonal neuropathy;Yang;Cell. Mol. Life Sci.,2007

4. Generalized giant axonal neuropathy: a filament-forming disease of neuronal, endothelial, glial, and schwann cells in a patient without kinky hair;Peiffer;Acta Neuropathol.,1977

5. New mutations, genotype phenotype studies and manifesting carriers in giant axonal neuropathy;Houlden;J. Neurol. Neurosurg. Psychiatry,2007

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