Enhanced Factor IX Activity following Administration of AAV5-R338L “Padua” Factor IX versus AAV5 WT Human Factor IX in NHPs-Reference-Cited by-同舟云学术

Enhanced Factor IX Activity following Administration of AAV5-R338L “Padua” Factor IX versus AAV5 WT Human Factor IX in NHPs

Published:2019-12 Issue: Volume:15 Page:221-231
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Spronck Elisabeth A.,Liu Ying Poi,Lubelski Jacek,Ehlert Erich,Gielen Sander,Montenegro-Miranda Paula,de Haan Martin,Nijmeijer Bart,Ferreira Valerie,Petry Harald,van Deventer Sander J.

Funder

uniQure

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

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