The engineered AAV2-HBKO promotes non-invasive gene delivery to large brain regions beyond ultrasound targeted sites
Author:
Publisher
Elsevier BV
Subject
Genetics,Molecular Biology,Molecular Medicine
Reference63 articles.
1. Single-dose gene-replacement therapy for spinal muscular atrophy;Mendell;N. Engl. J. Med.,2017
2. Intra-cisterna magna delivery of an AAV vector with the GLUT1 promoter in a pig recapitulates the physiological expression of SLC2A1;Nakamura;Gene Ther.,2021
3. Fourth boy dies in clinical trial of astellas’ AT132;Philippidis;Hum. Gene Ther.,2021
4. Targeted delivery of self-complementary adeno-associated virus serotype 9 to the brain, using magnetic resonance imaging-guided focused ultrasound;Thévenot;Hum. Gene Ther.,2012
5. Gene delivery to the spinal cord using MRI-guided focused ultrasound;Weber-Adrian;Gene Ther.,2015
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2. rAAV2-Mediated Restoration of GALC in Neural Stem Cells from Krabbe Patient-Derived iPSCs;Pharmaceuticals;2023-04-20
3. Sonoselective delivery using ultrasound and microbubbles combined with intravenous rAAV9 CLDN5-GFP does not increase endothelial gene expression;Gene Therapy;2023-02-13
4. Efficacy of gene delivery to the brain using AAV and ultrasound depends on serotypes and brain areas;Journal of Controlled Release;2022-11
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