Gene therapy for infantile malignant osteopetrosis: review of pre-clinical research and proof-of-concept for phenotypic reversal-Reference-Cited by-同舟云学术

Gene therapy for infantile malignant osteopetrosis: review of pre-clinical research and proof-of-concept for phenotypic reversal

Published:2021-03 Issue: Volume:20 Page:389-397
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Moscatelli Ilana^ORCID,Almarza Elena^ORCID,Schambach Axel,Ricks David,Schulz Ansgar,Herzog Christopher D.,Henriksen Kim,Askmyr Maria,Schwartz Jonathan D.,Richter Johan

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference81 articles.

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