Intracranial delivery of AAV9 gene therapy partially prevents retinal degeneration and visual deficits in CLN6-Batten disease mice-Reference-Cited by-同舟云学术

Intracranial delivery of AAV9 gene therapy partially prevents retinal degeneration and visual deficits in CLN6-Batten disease mice

Published:2021-03 Issue: Volume:20 Page:497-507
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

White Katherine A.,Nelvagal Hemanth R.,Poole Timothy A.,Lu Bin,Johnson Tyler B.,Davis Samantha,Pratt Melissa A.,Brudvig Jon,Assis Ana B.,Likhite Shibi,Meyer Kathrin,Kaspar Brian K.,Cooper Jonathan D.,Wang Shaomei,Weimer Jill M.^ORCID

Funder

Foundation for Barnes-Jewish Hospital

Washington University School of Medicine in St. Louis

National Institutes of Health

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

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