Micro-dystrophin gene therapy demonstrates long-term cardiac efficacy in a severe Duchenne muscular dystrophy model-Reference-Cited by-同舟云学术

Micro-dystrophin gene therapy demonstrates long-term cardiac efficacy in a severe Duchenne muscular dystrophy model

Published:2023-03 Issue: Volume:28 Page:344-354
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Piepho Arden B.,Lowe Jeovanna,Cumby Laurel R.,Dorn Lisa E.,Lake Dana M.,Rastogi Neha,Gertzen Megan D.,Sturgill Sarah L.,Odom Guy L.,Ziolo Mark T.,Accornero Federica,Chamberlain Jeffrey S.,Rafael-Fortney Jill A.

Funder

National Institutes of Health

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference24 articles.

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2. Cardiac pathophysiology and the future of cardiac therapies in Duchenne muscular dystrophy;Meyers;Int. J. Mol. Sci.,2019

3. Distinct pathophysiological mechanisms of cardiomyopathy in hearts lacking dystrophin or the sarcoglycan complex;Townsend;Faseb. J.,2011

4. Duchenne and Becker muscular dystrophy carriers: evidence of cardiomyopathy by exercise and cardiac MRI testing;Mah;Int. J. Cardiol.,2020

5. Progress toward gene therapy for Duchenne muscular dystrophy;Chamberlain;Mol. Ther.,2017

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