CRISPR-Cas9 correction in the DMD mouse model is accompanied by upregulation of Dp71f protein-Reference-Cited by-同舟云学术

CRISPR-Cas9 correction in the DMD mouse model is accompanied by upregulation of Dp71f protein

Published:2023-09 Issue: Volume:30 Page:161-180
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Egorova Tatiana V.,Polikarpova Anna V.,Vassilieva Svetlana G.,Dzhenkova Marina A.,Savchenko Irina M.,Velyaev Oleg A.,Shmidt Anna A.,Soldatov Vladislav O.,Pokrovskii Mikhail V.,Deykin Alexey V.,Bardina Maryana V.

Funder

Ministry of Education and Science of the Russian Federation

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

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1. Dystrophin- and Utrophin-Based Therapeutic Approaches for Treatment of Duchenne Muscular Dystrophy: A Comparative Review;BioDrugs;2023-11-02

2. Applications and Research Advances in the Delivery of CRISPR/Cas9 Systems for the Treatment of Inherited Diseases;International Journal of Molecular Sciences;2023-08-25