Micro-dystrophin AAV Vectors Made by Transient Transfection and Herpesvirus System Are Equally Potent in Treating mdx Mouse Muscle Disease-Reference-Cited by-同舟云学术

Micro-dystrophin AAV Vectors Made by Transient Transfection and Herpesvirus System Are Equally Potent in Treating mdx Mouse Muscle Disease

Published:2020-09 Issue: Volume:18 Page:664-678
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Hakim Chady H.,Clément Nathalie,Wasala Lakmini P.,Yang Hsiao T.,Yue Yongping,Zhang Keqing,Kodippili Kasun,Adamson-Small Laura,Pan Xiufang,Schneider Joel S.,Yang N. Nora,Chamberlain Jeffrey S.,Byrne Barry J.,Duan Dongsheng

Funder

U.S. Department of Defense

National Institutes of Health

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

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