Pathogenesis of Hepatic Tumors following Gene Therapy in Murine and Canine Models of Glycogen Storage Disease-Reference-Cited by-同舟云学术

Pathogenesis of Hepatic Tumors following Gene Therapy in Murine and Canine Models of Glycogen Storage Disease

Published:2019-12 Issue: Volume:15 Page:383-391
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Kang Hye-Ri,Gjorgjieva Monika,Smith Stephanie N.,Brooks Elizabeth D.,Chen Zelin,Burgess Shawn M.,Chandler Randy J.,Waskowicz Lauren R.,Grady Kylie M.,Li Songtao,Mithieux Gilles,Venditti Charles P.,Rajas Fabienne,Koeberl Dwight D.

Funder

Children's Fund for GSD Research

Children’s Miracle Network

Association for Glycogen Storage Disease

For the Love of Christopher

Alice and YT Chen Center for Pediatric Genetics and Genomics

French National Agency of Research

Association Francophone des Glycogénoses

National Institute of Diabetes and Digestive and Kidney Diseases

NIH

National Intramural Sequencing Center

Pfizer NC Biotechnology Gene Therapy

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

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