Dosing and Re-Administration of Lentiviral Vector for In Vivo Gene Therapy in Rhesus Monkeys and ADA-Deficient Mice-Reference-Cited by-同舟云学术

Dosing and Re-Administration of Lentiviral Vector for In Vivo Gene Therapy in Rhesus Monkeys and ADA-Deficient Mice

Published:2020-03 Issue: Volume:16 Page:78-93
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Carbonaro-Sarracino Denise A.,Tarantal Alice F.,Lee C. Chang I.,Kaufman Michael L.,Wandro Stephen,Jin Xiangyang,Martinez Michele,Clark Danielle N.,Chun Krista,Koziol Colin,Hardee Cinnamon L.,Wang Xiaoyan,Kohn Donald B.

Funder

National Institute of Allergy and Infectious Diseases

National Heart, Lung, and Blood Institute

Primate Center

Cores for Animal Care, Research Vectors, and Cell & Tissue Analysis

Eli and Edythe Broad Center for Regenerative Medicine & Stem Cell Research

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

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5. Correction of mucopolysaccharidosis type IIIA somatic and central nervous system pathology by lentiviral-mediated gene transfer;McIntyre;J. Gene Med.,2010

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