Flow-Cytometry Platform for Intracellular Detection of FVIII in Blood Cells: A New Tool to Assess Gene Therapy Efficiency for Hemophilia A-Reference-Cited by-同舟云学术

Flow-Cytometry Platform for Intracellular Detection of FVIII in Blood Cells: A New Tool to Assess Gene Therapy Efficiency for Hemophilia A

Published:2020-06 Issue: Volume:17 Page:1-12
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Elnaggar Muhammad,Al-Mohannadi Anjud,Kizhakayil Dhanya,Raynaud Christophe Michel,Al-Mannai Sharefa,Gentilcore Giusy,Pavlovski Igor,Sathappan Abbirami,Van Panhuys Nicholas,Borsotti Chiara,Follenzi Antonia,Grivel Jean-Charles,Deola Sara

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference39 articles.

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2. Gene therapy for the hemophilias;Kay;Proc. Natl. Acad. Sci. USA,1999

3. Gene therapy for hemophilia: what does the future hold?;Doshi;Ther. Adv. Hematol.,2018

4. AAV5–factor VIII gene transfer in severe hemophilia A;Rangarajan;N. Engl. J. Med.,2017

5. Intraosseous delivery of lentiviral vectors targeting factor VIII expression in platelets corrects murine hemophilia A;Wang;Mol. Ther.,2015

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1. Systematic Review on Flow Cytometry as a Versatile Tool for Disease Diagnosis;Current Pharmacology Reports;2024-07-03

2. CD14+/CD31+ monocytes expanded by UM171 correct hemophilia A in zebrafish upon lentiviral gene transfer of factor VIII;Blood Advances;2023-03-01

3. The Immune Response to the fVIII Gene Therapy in Preclinical Models;Frontiers in Immunology;2020-04-15