Safe and efficient in vivo hematopoietic stem cell transduction in nonhuman primates using HDAd5/35++ vectors
Author:
Funder
NIH
Bill & Melinda Gates Foundation
Publisher
Elsevier BV
Subject
Genetics,Molecular Biology,Molecular Medicine
Reference68 articles.
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3. Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ss-thalassemia;Marktel;Nat. Med.,2019
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5. Drug delivery systems for CRISPR-based genome editors;NAT REV DRUG DISCOV;2023
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