Thorough molecular configuration analysis of noncanonical AAV genomes in AAV vector preparations
Author:
Funder
U.S. Department of Health and Human Services
National Heart, Lung, and Blood Institute
NIH
Publisher
Elsevier BV
Reference36 articles.
1. Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: A randomised, controlled, open-label, phase 3 trial;Russell;Lancet,2017
2. Interindividual variability in transgene mRNA and protein production following adeno-associated virus gene therapy for hemophilia A;Fong;Nat. Med.,2022
3. Gene Therapy with Etranacogene Dezaparvovec for Hemophilia B;Pipe;N. Engl. J. Med.,2023
4. Gene therapy for spinal muscular atrophy (SMA): A review of current challenges and safety considerations for onasemnogene abeparvovec (Zolgensma);Ogbonmide;Cureus,2023
5. Etranacogene dezaparvovec for hemophilia B gene therapy;Thornburg;Ther. Adv. Rare Dis.,2021
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