Inhibition of DNA-dependent protein kinase catalytic subunit boosts rAAV transduction of polarized human airway epithelium
Author:
Funder
NIAID
NIDDK
University of Iowa
National Institutes of Health
Publisher
Elsevier BV
Subject
Genetics,Molecular Biology,Molecular Medicine
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1. SP-101, A Novel Adeno-Associated Virus Gene Therapy for the Treatment of Cystic Fibrosis, Mediates Functional Correction of Primary Human Airway Epithelia From Donors with Cystic Fibrosis;Human Gene Therapy;2024-08-29
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