Subject
Genetics,Molecular Biology,Molecular Medicine
Reference19 articles.
1. 2021 Guidelines for the Management of Transfusion Dependent Thalassemia;Cappellini,2021
2. Beta-thalassemia;Galanello;Orphanet J. Rare Dis.,2010
3. Gene Addition Strategies for β-Thalassemia and Sickle Cell Anemia;Dong,2017
4. Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia;Thompson;N. Engl. J. Med.,2018
5. Betibeglogene Autotemcel Gene Therapy for Non–β0/β0 Genotype β-Thalassemia;Locatelli;N. Engl. J. Med.,2022